Category:Orphan drugs
From HandWiki
Here is a list of articles in the Orphan drugs category of the Chemistry portal.
Lists of all drugs that have received orphan status in the United States and Europe are available from the U.S. Food and Drug Administration and the European Commission, respectively:
Pages in category "Orphan drugs"
The following 200 pages are in this category, out of 307 total.
(previous page) (next page)A
- Biology:Acalabrutinib
- Chemistry:Acetohydroxamic acid
- Chemistry:Adagrasib
- Chemistry:Afamelanotide
- Chemistry:Afatinib
- Chemistry:Afegostat
- Chemistry:Alglucosidase alfa
- Chemistry:Alisporivir
- Chemistry:Alpha-1 antitrypsin
- Chemistry:Altretamine
- Chemistry:Alvocidib
- Chemistry:Amatuximab
- Chemistry:Ambrisentan
- Chemistry:Amikacin
- Chemistry:4-Aminopyridine
- Chemistry:Amitriptyline
- Chemistry:Anagrelide
- Chemistry:Ansuvimab
- Chemistry:Anti-CD22 immunotoxin
- Biology:Arylsulfatase B
- Biology:Asfotase alfa
- Chemistry:Ataluren
- Chemistry:Atezolizumab
- Chemistry:Avapritinib
- Chemistry:Avatrombopag
- Chemistry:Avelumab
- Biology:Axicabtagene ciloleucel
- Chemistry:Azacitidine
B
- Chemistry:Bardoxolone methyl
- Chemistry:Belantamab mafodotin
- Chemistry:Belimumab
- Chemistry:Belumosudil
- Chemistry:Belzutifan
- Chemistry:Benralizumab
- Chemistry:Berotralstat
- Chemistry:Bevacizumab
- Chemistry:Bortezomib
- Chemistry:Brentuximab vedotin
- Biology:Brexucabtagene autoleucel
- Chemistry:Brigatinib
- Chemistry:Brincidofovir
- Biology:Bromelain (pharmacology)
- Chemistry:Bulevirtide
- Chemistry:Burosumab
- Chemistry:Busulfan
C
- Chemistry:C-Met inhibitor
- Chemistry:Caffeine citrate
- Chemistry:Calaspargase pegol
- Chemistry:Cannabidiol
- Chemistry:Caplacizumab
- Chemistry:Capmatinib
- Chemistry:Carboprost
- Chemistry:Carglumic acid
- Chemistry:Carmustine
- Chemistry:Catridecacog
- Chemistry:Cerliponase alfa
- Biology:CGTG-102
- Chemistry:Chlormethine
- Chemistry:Cholic acid
- Chemistry:Cilengitide
- Biology:Ciltacabtagene autoleucel
- Chemistry:Cladribine
- Chemistry:Clofazimine
- Chemistry:Cobicistat
- Chemistry:Cobimetinib
- Chemistry:Colchicine
- Chemistry:Collagenase clostridium histolyticum
- Chemistry:Copper (64Cu) oxodotreotide
- Biology:Crizanlizumab
- Chemistry:Cromoglicic acid
- Chemistry:Cysteamine
D
E
- Chemistry:Eculizumab
- Chemistry:Edaravone
- Chemistry:Efgartigimod alfa
- Chemistry:Elafibranor
- Chemistry:Elapegademase
- Chemistry:Elesclomol
- Chemistry:Elexacaftor
- Chemistry:Elotuzumab
- Chemistry:Eltrombopag
- Chemistry:Emapalumab
- Chemistry:Enasidenib
- Chemistry:Entinostat
- Chemistry:Enzastaurin
- Chemistry:Eribulin
- Chemistry:Erlotinib
- Chemistry:Estetrol
- Chemistry:Evinacumab
F
G
I
- Chemistry:Ibalizumab
- Chemistry:Ibrutinib
- Chemistry:Ibutamoren
- Chemistry:Icatibant
- Biology:Idecabtagene vicleucel
- Biology:Iduronidase
- Chemistry:Idursulfase
- Chemistry:Imatinib
- Chemistry:Imiglucerase
- Chemistry:Imlifidase
- Chemistry:Immunomodulatory imide drug
- Biology:Inclisiran
- Chemistry:Inebilizumab
- Chemistry:IRGD
- Chemistry:Isatuximab
- Chemistry:Istiratumab
- Chemistry:Itraconazole
- Chemistry:Ivacaftor
- Chemistry:Ivosidenib
- Chemistry:Ixazomib
L
- Chemistry:Lanadelumab
- Chemistry:Larotrectinib
- Chemistry:Lenacapavir
- Chemistry:Lenvatinib
- Chemistry:Lintuzumab
- Biology:Lisocabtagene maraleucel
- Chemistry:Lithium carbonate
- Chemistry:Lomitapide
- Chemistry:Lonafarnib
- Chemistry:Loncastuximab tesirine
- Chemistry:Lorlatinib
- Chemistry:Losmapimod
- Chemistry:Lumacaftor
- Biology:Lumasiran
- Chemistry:Lurbinectedin
- Biology:Luspatercept
- Chemistry:Lusutrombopag
- Chemistry:Lutetium (177Lu) oxodotreotide
M
- Chemistry:Margetuximab
- Chemistry:Maribavir
- Chemistry:Mecasermin rinfabate
- Chemistry:Melphalan
- Chemistry:Melphalan flufenamide
- Chemistry:Mepolizumab
- Chemistry:Metformin
- Chemistry:Methotrexate
- Chemistry:Methoxsalen
- Chemistry:Metreleptin
- Chemistry:Mifamurtide
- Chemistry:Miglustat
- Chemistry:Mitapivat
- Biology:Mitomycin C
- Chemistry:Mitotane
- Chemistry:Mobocertinib
- Chemistry:Mogamulizumab
- Chemistry:Moxetumomab pasudotox
- Chemistry:Moxidectin